Hosted by the Propionic Acidemia Foundation and The Community Health Clinic, this conference is dedicated to finding better treatments and a cure for Propionic Acidemia. The Propionic Acidemia Foundation supports this mission by funding research and providing vital information and support to families and medical professionals.
The Butterfly Gala is an annual fundraising event to raise awareness and funds for pediatric cancer Rhabdomyosarcoma research, provide financial assistance for families while their children are undergoing treatment and […]
The World Orphan Drug Congress is the largest and most established global meeting focused on orphan drugs and rare diseases. It covers topics such as cell and gene therapy, genetic testing, market access, real-world evidence, and orphan drug policy. With over 130 leading solution providers from around the world, the congress showcases new ways of […]
The Advanced Therapies Congress will feature speakers from across the entire value chain of cell and gene therapy development, offering 8 tracks of content over 2 days. Attendees can engage with 50 leading solution providers to support all stages of cell and gene therapy development. Additionally, there will be opportunities to connect with thousands of […]
The 2024 FOXG1 Syndrome Parents Conference will be held November 15th-17th, 2024 at the Marriott Resort Fort Lauderdale Pompano Beach. In this retreat setting, FOXG1 parents will connect with other FOXG1 parents, scientists, and leading FOXG1 clinicians to learn about the spectrum of FOXG1 syndrome, the FOXG1 research strategy towards a cure, and parenting children […]
Join us for a morning of connecting with other mothers also navigating the journey of raising children with neurodivergence and other rare diagnoses. This space is crafted for meaningful conversations around finding authentic support and recharging your battery as a caregiver. Think of this morning as an opportunity to reconnect with yourself, fill your cup, […]
RAREfest24, a scientific, educational, and community-centric event, is scheduled for November 22 and 23 at the Guildhall in Cambridge. This 2-day festival celebrates rare diseases with interactive talks, demos, exhibits, film, and art, highlighting innovative science, visionary technology, and pioneering organizations that bring hope to those affected. RAREfest is a biannual event aiming to shift […]
The AES Annual Meeting stands as the foremost gathering for healthcare providers, scientists, advocates, industry professionals, and others committed to improving outcomes for individuals with epilepsy. This event features five […]
Join the National MPS Society for their 38th Annual Family and Scientific Conference as they celebrate 50 years! This milestone event will feature speakers from across the country addressing the […]
The World Orphan Drug Congress brings together leaders from pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors, and solution providers. This conference serves as a […]
